Last week, Families of SMA congratulated the Gaynor Family of New York on their amazing fundraising and SMA awareness success. Families of SMA and the Gaynors have partnered up to raise funds for the final stages needed to ask the FDA for approval to begin clinical trials with the SMA stem cell program and to try and accelerate the program. The research team is now preparing for the final steps before meeting with the FDA to request approval to move forward toward the critical clinical trials in patients. The Gaynors, through Sophia’s Cure, will be attempting to raise a total of $200,000 specifically for the SMA Motor Neuron Replacement Program. Families of SMA will then attempt to meet this sum by raising additional donations for the program. Our efforts through Unite For The Cure will be going to help Families of SMA raise these additional funds.
Click here or on the article below to read more about this on the Families of SMA website…
